WHO ICTRP trial

Long-term observational study of Gene Therapy for AADC deficiency

JPRN-jRCT2033220245 · Japan Primary Registries Network (JPRN) · Recruiting

Key facts

Trial ID JPRN-jRCT2033220245
Public title Long-term observational study of Gene Therapy for AADC deficiency
Scientific title Long-term observational study of Gene Therapy for AADC deficiency
Primary sponsor Yamagata Takanori
Secondary sponsors Gene Therapy Research Institution Co., Ltd.
Registry Japan Primary Registries Network (JPRN)
Recruitment status Recruiting
Study type Observational
Conditions Aromatic L-amino acid decarboxylase deficiency
Registration date May 8, 2022
Target size 1
Registry page jrct.niph.go.jp

At a glance

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Source: World Health Organization (WHO), International Clinical Trials Registry Platform (ICTRP) · Source date:

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