WHO ICTRP trial
An open label, single arm IIT clinical study evaluating the safety…
ChiCTR2500095667 · Chinese Clinical Trial Registry (ChiCTR) · Not Recruiting
Key facts
| Trial ID | ChiCTR2500095667 |
|---|---|
| Public title | An open label, single arm IIT clinical study evaluating the safety, tolerability, and preliminary efficacy of GCB-001 in the treatment of patients with delayed onset type 2 SMA who can sit alone but cannot walk |
| Scientific title | An open label, single arm IIT clinical study evaluating the safety, tolerability, and preliminary efficacy of GCB-001 in the treatment of patients with delayed onset type 2 SMA who can sit alone but cannot walk |
| Primary sponsor | The Children's Hospital of Zhejiang University School of Medicine |
| Registry | Chinese Clinical Trial Registry (ChiCTR) |
| Recruitment status | Not Recruiting |
| Study type | Interventional study |
| Phase | 1 |
| Countries | China |
| Conditions | Spinal muscular atrophy |
| Interventions | Low Dosing group:Intrathecal injection Low Dosing GCB-001;High Dosing group:Intrathecal injection High Dosing GCB-001 |
| Registration date | Jan 10, 2025 |
| Target size | Low Dosing group:3;High Dosing group:3 |
| Registry page | chictr.org.cn |
At a glance
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About WHO ICTRP trial registrations
The WHO ICTRP combines trial registrations from primary registries worldwide into a single searchable index. Contact and ethics-committee details are not shown here.
Source: World Health Organization (WHO), International Clinical Trials Registry Platform (ICTRP) · Source date: