Clinical trial
Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular…
NCT00494195 · Nationwide Children's Hospital, Other · Completed
Key facts
| NCT number | NCT00494195 |
|---|---|
| Title | Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) |
| Official title | Phase I Gene Transfer of rAAV1.tMCK.Human-alpha-sarcoglycan for Limb Girdle Muscular Dystrophy Type 2D (LGMD2D) |
| Lead sponsor | Nationwide Children's Hospital, Other |
| Collaborators | National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) NIH Muscular Dystrophy Association |
| Status | Completed |
| Phase | Phase 1 |
| Study type | Interventional |
| Conditions | Muscular Dystrophies |
| Intervention type | Genetic |
| Interventions | rAAV1.tMCK.human-alpha-sarcoglycan- First cohort, Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- Second cohort |
| Enrollment | 6 |
| Start date | Mar 1, 2008 |
| Primary completion | Jun 1, 2011 |
| Completion | Aug 1, 2011 |
| First posted | Jun 29, 2007 |
| Last update posted | Feb 5, 2013 |
| Countries | United States |
At a glance
- 1–9 Study sites
- No Results posted
- None Linked FDA submissions
Counts are shown as ranges. Exact figures, trends and every underlying record are available in Orca1.
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Source: U.S. National Library of Medicine (NLM), ClinicalTrials.gov · Source date: