Clinical trial
Experimental Gene Transfer Procedure to Treat Alpha 1-Antitrypsin Deficiency
NCT00377416 · University of Massachusetts, Worcester, Other · Completed
Key facts
| NCT number | NCT00377416 |
|---|---|
| Title | Experimental Gene Transfer Procedure to Treat Alpha 1-Antitrypsin Deficiency |
| Official title | Preclinical & Phase I/II Trials of AAV-AAT Vectors: Phase I Trial of Intramuscular Injection of a Recombinant Adeno-Associated Virus Alpha 1-Antitrypsin (rAAV2-CB-hAAT) Gene Vector to AAT-Deficient Adults |
| Lead sponsor | University of Massachusetts, Worcester, Other |
| Collaborators | National Heart, Lung, and Blood Institute (NHLBI) NIH Alpha-1 Foundation University of Florida National Center for Research Resources (NCRR) |
| Status | Completed |
| Phase | Early Phase 1 |
| Study type | Interventional |
| Conditions | Alpha 1-Antitrypsin Deficiency |
| Intervention type | Genetic |
| Interventions | rAAV2-CB-hAAT Gene Vector |
| Enrollment | 12 |
| Start date | Mar 1, 2004 |
| Primary completion | Oct 1, 2006 |
| Completion | Jan 1, 2020 |
| First posted | Sep 18, 2006 |
| Last update posted | Apr 10, 2020 |
| Countries | United States |
At a glance
- 1–9 Study sites
- No Results posted
- None Linked FDA submissions
Counts are shown as ranges. Exact figures, trends and every underlying record are available in Orca1.
About ClinicalTrials.gov studies
ClinicalTrials.gov is the U.S. National Library of Medicine's registry of clinical studies conducted around the world. Contact and investigator details are not shown here.
Source: U.S. National Library of Medicine (NLM), ClinicalTrials.gov · Source date: