Clinical trial
Safety Study of a Gene Transfer Vector for Children With Late Infantile Neuronal…
NCT00151216 · Weill Medical College of Cornell University, Other · Completed
Key facts
| NCT number | NCT00151216 |
|---|---|
| Title | Safety Study of a Gene Transfer Vector for Children With Late Infantile Neuronal Ceroid Lipofuscinosis |
| Official title | Administration of a Replication Deficient Adeno-associated Virus Gene Transfer Vector Expressing the Human CLN2 cDNA to the Brain of Children With Late Infantile Neuronal Ceroid Lipofuscinosis |
| Lead sponsor | Weill Medical College of Cornell University, Other |
| Collaborators | Nathan's Battle Foundation |
| Status | Completed |
| Phase | Phase 1 |
| Study type | Interventional |
| Conditions | Batten Disease, Late Infantile Neuronal Ceroid Lipofuscinosis |
| Intervention type | Biological |
| Interventions | AAV2CUhCLN2 (3x10^12 particle units) |
| Enrollment | 10 |
| Start date | Jun 1, 2004 |
| Primary completion | Jun 1, 2019 |
| Completion | Jun 1, 2019 |
| First posted | Sep 8, 2005 |
| Last update posted | Jul 24, 2020 |
| Countries | United States |
At a glance
- 1–9 Study sites
- No Results posted
- None Linked FDA submissions
Counts are shown as ranges. Exact figures, trends and every underlying record are available in Orca1.
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Source: U.S. National Library of Medicine (NLM), ClinicalTrials.gov · Source date: