Clinical trial

Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to…

NCT00018018 · National Human Genome Research Institute (NHGRI), NIH · Completed

Key facts

NCT number NCT00018018
Title Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency
Official title Treatment of SCID Due to ADA Deficiency With Autologous Cord Blood or Bone Marrow CD34+ Cells Transduced With a Human ADA Gene
Lead sponsor National Human Genome Research Institute (NHGRI), NIH
Status Completed
Phase Phase 1
Study type Interventional
Conditions Severe Combined Immunodeficiency Syndrome
Intervention type Drug
Interventions CD34+ cells transduced with ADA retrovir
Enrollment 8
Start date Jun 20, 2001
Completion Sep 17, 2014
First posted Jun 28, 2001
Last update posted Dec 12, 2019
Countries United States

At a glance

  • 1–9 Study sites
  • No Results posted
  • None Linked FDA submissions

Counts are shown as ranges. Exact figures, trends and every underlying record are available in Orca1.

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