Clinical trial

Gene Therapy for the Treatment of Fanconi's Anemia Type C

NCT00001399 · National Heart, Lung, and Blood Institute (NHLBI), NIH · Completed

Key facts

NCT number NCT00001399
Title Gene Therapy for the Treatment of Fanconi's Anemia Type C
Official title Retroviral Mediated Gene Transfer of the Fanconi Anemia Complementation Group C Gene to Hematopoietic Progenitors of Group C Patients
Lead sponsor National Heart, Lung, and Blood Institute (NHLBI), NIH
Status Completed
Phase Phase 1
Study type Interventional
Conditions Fanconi's Anemia, Pancytopenia
Intervention type Drug
Interventions Transduced CD34+ Cells
Enrollment 9
Start date Dec 3, 1993
Completion Feb 11, 2009
First posted Nov 4, 1999
Last update posted Jul 2, 2017
Countries United States

At a glance

  • 1–9 Study sites
  • No Results posted
  • None Linked FDA submissions

Counts are shown as ranges. Exact figures, trends and every underlying record are available in Orca1.

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