Clinical trial
Gene Therapy for Gaucher's and Fabry Disease Using Viruses and Blood-Forming…
NCT00001234 · National Institute of Neurological Disorders and Stroke (NINDS), NIH · Completed
Key facts
| NCT number | NCT00001234 |
|---|---|
| Title | Gene Therapy for Gaucher's and Fabry Disease Using Viruses and Blood-Forming Cells |
| Official title | Retroviral-Mediated Transfer and Expression of Glucocerebrosidase and Ceramidtrihexosidase (a-Galactosidase A) cDNA's in Human Hematopoietic Progenitor Cells |
| Lead sponsor | National Institute of Neurological Disorders and Stroke (NINDS), NIH |
| Status | Completed |
| Phase | Phase 1 |
| Study type | Interventional |
| Conditions | Gaucher's Disease |
| Intervention type | Genetic |
| Interventions | human glucocerebrosidase cDNA |
| Enrollment | 120 |
| Start date | Jan 1, 1988 |
| Completion | Apr 1, 2002 |
| First posted | Nov 4, 1999 |
| Last update posted | Mar 4, 2008 |
| Countries | United States |
At a glance
- 1–9 Study sites
- No Results posted
- None Linked FDA submissions
Counts are shown as ranges. Exact figures, trends and every underlying record are available in Orca1.
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Source: U.S. National Library of Medicine (NLM), ClinicalTrials.gov · Source date: